smanewstoday.com
Gene Therapy Delivered By Virus Shows Promise For Treating Spinal Muscular Atrophy (SMA)
http://smanewstoday.com/2014/12/23/gene-therapy-delivered-virus-shows-promise-treating-spinal-muscular-atrophy-sma
This is a short description about myself and what this site is about. I hope you enjoy being here! SMN Gene Therapy (Genzyme Sanofi). SMN Gene Therapy (Genethon Inserm). Spinal Muscular Atrophy Overview. Spinal Muscular Atrophy Type 0. Spinal Muscular Atrophy Type 1. Spinal Muscular Atrophy Type 2. Spinal Muscular Atrophy Type 3. Spinal Muscular Atrophy Type 4. Spinal Muscular Atrophy Diagnosis. Spinal Muscular Atrophy Symptoms. Poor Muscle Tone / Muscle Weakness. Spinal Muscular Atrophy and Scoliosis.
wms2015.com
WMS 2015: Sponsors
http://www.wms2015.com/index.php/sponsors
Abstract notifications have been sent out. View the Pre-Congress Course Programme. Click here to find out more about UK Visa Regulations. The Annual Congress of the World Muscle Society (WMS) is the premier annual international Congress on neuromuscular disorders. The approximately 550 attendees at the Congress include the key individuals from around the world currently working in the field of neuromuscular disease diagnosis and research. If you have any questions. TERMS AND CONDITIONS.
asi-sma.blogspot.com
Spinal Muscular Atrophy ,SMA izomsorvadás,: október 2014
http://asi-sma.blogspot.com/2014_10_01_archive.html
Spinal Muscular Atrophy ,SMA izomsorvadás,. 2014 október 4., szombat. 2014-október-2 Dallas. AveXis Inc. Bejelentette, hogy az Amerikai Food and Drug Administration (FDA) megadta az engedélyt a scAAV9 gyógyszer jelöltre a SMA-izomsorvadásba. Itt olvashatsz a kísérletekről: http:/ asi-sma.blogspot.hu/2014/04/scaav9-cbsmn-gen.html. A bejegyzésre mutató linkek. 2014 október 2., csütörtök. Svájci gyógyszeripari vállalat Hoffmann-La Roche bejelentette, hogy rövidesen meg kezdi az első fázisú RO6885247.
asi-sma.blogspot.com
Spinal Muscular Atrophy ,SMA izomsorvadás,: Génterápia.
http://asi-sma.blogspot.com/2014/10/genterapia.html
Spinal Muscular Atrophy ,SMA izomsorvadás,. 2014 október 4., szombat. 2014-október-2 Dallas. AveXis Inc. Bejelentette, hogy az Amerikai Food and Drug Administration (FDA) megadta az engedélyt a scAAV9 gyógyszer jelöltre a SMA-izomsorvadásba. Itt olvashatsz a kísérletekről: http:/ asi-sma.blogspot.hu/2014/04/scaav9-cbsmn-gen.html. Feliratkozás: Megjegyzések küldése (Atom). Keresés ebben a blogban.
pbmcap.com
Avexis - PBM Capital Group
http://www.pbmcap.com/portfolio-companies/avexis
Based in Dallas, Texas, AveXis is a clinic-ready, synthetic biology platform company. AveXis has, at its core, a desire to establish unique industry and research alliances which will bring innovative treatments to people with unmet medical needs. Our work in spinal muscular atrophy (SMA), a rare/orphan disease, is our first focus. The name AveXis is derived from a combination of scientific terms involved in our work, in addition to a mythological figure:. Av = adeno-associated virus (AAV). X = DNA helix.
pbmcap.com
AveXis Closes a Round of Financing from PBM Capital to Advance its SMA Gene Therapy Program - PBM Capital Group
http://www.pbmcap.com/avexis-closes-a-round-of-financing-from-pbm-capital-to-advance-its-sma-gene-therapy-program
AveXis Closes a Round of Financing from PBM Capital to Advance its SMA Gene Therapy Program. Securing this capital not only provides AveXis with additional resources to advance its SMA gene therapy program both commercially and clinically but also aligns well with the company’s strategy of integrating entrepreneurship and philanthropy, said Mindy Du, Director of Scientific and Corporate Affairs at AveXis. This trial represents the best of bench-to-bedside translational research. Dr. Mendell and h...With ...
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